Presentations

2017

Susanne Urach, et al. Statistical properties of hypothesistests using Goal Attainment Scaling
CEN-ISBS, Vienna, Austria
Kit Roes. Clinical trials in rare diseases:there is no magic potion.
CEN-ISBS, Vienna, Austria
Charlotte Gaasterland. Rare diseases: Methodology and other challenges
IFMSA I AM Summerschool, Amsterdam, the Netherlands
Susanne Urach, et al. Statistical properties of hypothesis tests using Goal Attainment Scaling.
ISCB 37, Vigo, Spain
Charlotte Gaasterland. Goal Attainment Scaling: a potential way forward
ICTMC, Liverpool, UK
Hanneke van der Lee. Patient centered outcome measurements in rare disease trials: Challenges and potential solutions
ICTMC, Liverpool, UK
Susanne Urach, et al. Statistical properties of hypothesis tests using Goal Attainment Scaling.
ICTMC, Liverpool, UK
Hanneke van der Lee. Pharmacotherapy in children – small populations of human subjects who are not just small adults.
InSPiRe conference, Coventry, UK
Hanneke van der Lee. Goal Attainment Scaling, an individualized instrument with potential for outcome measurement in rare diseases
Duke-Margolis Center for Health Policy , Washington DC, US
Charlotte Gaasterland, Hanneke van der Lee. Het Asterix project: methodologie van onderzoek bij zeldzame ziekten
PGO Support, Utrecht, The Netherlands

2016

Kit Roes. Directions for new developments on statistical design and analyses of small population group trials.
FIGON, Amsterdam, The Netherlands
Martin Posch. Evidence, Eminence and Extrapolation - An extrapolation framework to specify requirements for drug development in children.
Joint Conference of IEA-EEF, EFMI, DGEpi, GMDS, Munich, Germany
Susanne Urach, Martin Posch. Multi-arm group sequential designs with a simultaneous stopping rule.
JSM 2016 Chicago, USA - Biopharmaceutical Student Paper Award 2016 of the American Statistical Association
Robin Ristl, Dong Xi, Ekkehard Glimm, Martin Posch, Optimal exact tests for multiple binary endpoints.
ISCB 37, Birmingham, UK
Hanneke van der Lee. Goal Attainment Scaling, an individualised instrument with potential for outcome measurement in rare diseases,
FIGON, Ede, The Netherlands
Susanne Urach, Martin Posch. Multi-arm group sequential designs with a simultaneous stopping rule. ICODOE 2016, Memphis, USA
Hanneke van der Lee. Better design of clinical research for orphan diseases and the patient perspective. ECDR, Edinburgh, UK
Robin Ristl, Dong Xi, Ekkehard Glimm, Martin Posch, Optimal exact tests for multiple binary endpoints. International Statistics Festival Salzburg, Salzburg, Austria
Hanneke van der Lee. Promoting clinical development for patients with rare diseases: an overview of new methodology by the Asterix project.
Orphan Drugs Summit, Hoofddorp, The Netherlands
Egbert Biesheuvel. Advances in Small Trials dEsign for Regulatory Innovation and eXcellence.
ePharma Day, Milana, Italy
Martin Posch. Evidence, Eminence and Extrapolation - An extrapolation framework to specify requirements for drug development in children.
Bayes, Leuven, Belgium
Robin Ristl, Dong Xi, Ekkehard Glimm, Martin Posch. Optimal exact tests for multiple binary endpoints. Adaptive Designs and Multiple Comparison Procedures Workshop, Padua, Italy
Martin Posch. An extrapolation framework to specify requirements for drug development in children.
DIA/FDA Statistics Forum, North Bethesda, US

2015

Martin Posch. Addressing multiple objectives in clinical trials: Adaptive designs and multiple testing. University of Lancaster, UK
Martin Posch. An extrapolation framework to specify requirements for drug development in children.
Clinical trials in small population Workshop, London, UK
Susanne Urach, Martin Posch. Group sequential designs for clinical trials with multiple treatment arms.
WBS seminar, Vienna, Austria
Martin Posch. How to weight the strength of prior information and clarify the expected level of evidence? EMA expert workshop on extrapolation across age groups, London, UK
Martin Posch. Optimized stopping rules for multi-arm group sequential designs.
9th MCP Conference, Hyderabad, India
Susanne Urach, Martin Posch. Group sequential designs for clinical trials with multiple treatment arms.
8th International Workshop on Simulation, Vienna, Austria
Kit Roes. Advances in Small Trials dEsign for Regulatory Innovation and eXcellence.
ISCB 36, Utrecht, the Netherlands
Armin Koch. The role of subgroups in confirmatory clinical trials for drug licensing.
ISCB 36, Utrecht, the Netherlands
Robin Ristl, Florian Frommlet, Armin Koch, Martin Posch Fallback tests for co-primary endpoints.
ISCB 36, Utrecht, the Netherlands
Ingeborg van der Tweel, Putri Novianti, Konstantinos Pateras, Kit Roes Strategies for dealing with heterogeneity between studies in rare diseases.
ISCB 36, Utrecht, the Netherlands
Charlotte Gaasterland. Systematic review of Goal Attainment Scaling as an outcome measure in drug trials.
ISCB 36, Utrecht, the Netherlands
Robin Ristl, Posch Optimal rejection regions for testing multiple binary endpoints in small samples.
Adaptive Designs and Multiple Comparison Procedures Workshop, Köln, Germany
Susanne Urach, Martin Posch Group sequential designs for clinical trials with multiple treatment arms.
Joint Working Group of the ROeS and German Region of IBS, Köln, Germany
Robin Ristl, Florian Frommlet, Armin Koch, Martin Posch Fallback tests for co-primary endpoints.
ICSA Applied Statistical Symposium, Fort Collins, Colorado, USA
Susanne Urach, Martin Posch Group sequential designs for clinical trials with multiple treatment arms. Symposium on Early Phase Dose Finding Methodology, Paris, France
Robin Ristl, Florian Frommlet, Armin Koch, Martin Posch A Parametric Rüger Test for Testing Multiple Co-Primary Endpoints
Austria-Japan Joint Statistics Workshop, Osaka, Japan
Martin Posch, Trends in adaptive design and statistical approaches to small population group trials in EU. PMDA, Tokyo, Japan
Martin Posch. Industry’s perspective of the progress made implementing adaptive trials and the potential for the future.
Joint Adaptive Design and Bayesian Statistics Conference: Drivers of Efficiency in Modern Medical Product Development, Arlington, USA